• Achondroplasia,  BioMarin

    BioMarin – Update for Achondroplasia Associations

    As more cases of COVID-19 are confirmed, we recognize the increased challenges and concerns faced by participants in the BioMarin clinical studies. The safety and well-being of study participants, healthcareproviders, and our communities is paramount as the ongoing COVID-19 pandemic impacts the health and livelihoods of many worldwide. BioMarin Pharmaceutical, Inc., April 2020 Click here for full report.

  • Achondroplasia

    Little legend: Child with rare form of dwarfism begins his biggest adventure yet

    A child’s first day of school can be a daunting experience – both for the new student and their anxious parents. But when your child is just a little bit different – like five-year-old Floyd Henry Morley – the first day of school brings with it a whole new host of challenges.  Floyd was born with a rare form of dwarfism called Achondroplasia. People with Achondroplasia typically have short arms and legs, an enlarged head and an average-sized torso. 60 Minutes first met Floyd and his family in 2014 when he was just 5 months old. After the initial shock of Floyd’s diagnosis – which came completely at random –…

  • Achondroplasia

    #RareDiseaseDay 2019

    Out now – new official #RareDiseaseDay video! Watch Filip and Alina’s story. He is from Romania and lives with achondroplasia Share the video to raise awareness of rare diseases for Rare Disease Day 2019. #ShowYourRare Rare disease day is on February 28!