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2026 ACHONDROPLASIA & SKELETAL DYSPLASIA RESEARCH CONFERENCE • ORLANDO, FL

FRIDAY, MAY 22- SUNDAY, MAY 24
The Chandler Project
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The Chandler Project

5 YEARS OF AGE AND OLDER

  • RIBOMIC Announces Positive Interim Results from Phase IIa Trial of umedaptanib pegol in Achondroplasia Demonstrating Increase in Annualized Growth Rate of up to +4.6 cm/year in Children 5 Years of Age and Older in the Low Dose Cohort
    Clinical Trial · RIBOMIC · Umedaptanib Pego

    RIBOMIC Announces Positive Interim Results from Phase IIa Trial of umedaptanib pegol in Achondroplasia Demonstrating Increase in Annualized Growth Rate of up to +4.6 cm/year in Children 5 Years of Age and Older in the Low Dose Cohort

    Source: BioSpace® TOKYO–(BUSINESS WIRE)–RIBOMIC, Inc. (TOKYO:4591), a clinical-stage pharmaceutical company specializing in aptamer therapeutics, has been conducting a Phase IIa clinical trial of umedaptanib pegol (anti-FGF2 aptamer) in pediatric patients…

    Read More RIBOMIC Announces Positive Interim Results from Phase IIa Trial of umedaptanib pegol in Achondroplasia Demonstrating Increase in Annualized Growth Rate of up to +4.6 cm/year in Children 5 Years of Age and Older in the Low Dose CohortContinue

  • U.S. Food and Drug Administration Approves BioMarin’s VOXZOGO® (vosoritide) for Children Under 5 Years with Achondroplasia
    Achondroplasia · BioMarin · Hypochondroplasia · Voxzogo

    U.S. Food and Drug Administration Approves BioMarin’s VOXZOGO® (vosoritide) for Children Under 5 Years with Achondroplasia

    The following press release was obtained from BioMarin.com. To learn more about BioMarin, VOXZOGO®, vosorotide, and their other pipelines and research for achondroplasia and other skeletal dysplasias, click here. Expanded…

    Read More U.S. Food and Drug Administration Approves BioMarin’s VOXZOGO® (vosoritide) for Children Under 5 Years with AchondroplasiaContinue

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    • ABOUT
      • MISSION
      • FOUNDER’S STORY
    • COMMUNITY
      • Friends of Chandler
      • RARE-X
      • PICNIC HEALTH
      • THE MIGHTY
    • CONDITIONS
      • ACHONDROPLASIA
      • HYPOCHONDROPLASIA
      • PSEUDOACHON.
      • SEDC
    • PHARMACHON
      • Nurse Vic’s Notes
    • RESEARCH
      • NEWS
      • STUDIES & TRIALS
      • Treatments & Pipelines
        • BioMarin Pharmaceutical
        • QED Therapeutics
        • Ascendis Pharma
        • Tyra Biosciences
        • SANOFI
        • INNOSKEL
        • PFIZER (NULL)
    • CONTACT
    Search