Achondroplasia

Growing Strong

Bay Area parents Munira and Amer Haider talk about the fund they established to help support research on Achondroplasia,... Read More
Achondroplasia

Lower limb biomechanics during gait in children with Achondroplasia

via Journal of Biomechanics.Damien Kiernan – dkiernan@crc.ie Movement Analysis Laboratory, Central Remedial Clinic, Clontarf, Dublin 3, Ireland AbstractAchondroplasia is... Read More
BioMarin

BioMarin Announced Positive Final Results from Vosoritide Phase 3 pivotal trial. (BMN111-301)

BioMarin Announces Positive Final Results from Placebo-Controlled Phase 3 Data in Children with Achondroplasia Treated with Vosoritide Placebo-adjusted Increase... Read More
Achondroplasia

Think Beyond the Extremities – Complications in Skeletal Dysplasia

Watch the LLRS 2019 Presidential Guest Lecture: Think Beyond the Extremities – Complications in Skeletal Dysplasia by William G.... Read More
Ascendis

Ascendis Pharma Announces Orphan Drug Designation Granted for TransCon CNP as Treatment for Achondroplasia

COPENHAGEN, Denmark, Feb. 28, 2019 (GLOBE NEWSWIRE) — Ascendis Pharma A/S (Nasdaq: ASND), a biopharmaceutical company that utilizes its innovative TransCon™ technology to address... Read More
Achondroplasia

#RareDiseaseDay 2019

Out now – new official #RareDiseaseDay video! Watch Filip and Alina’s story. He is from Romania and lives with achondroplasia Share the video... Read More
Achondroplasia

The Chandler Project

As our first project, we are currently working on a weekend event dedicated to learning about new research and... Read More
Limb Lengthening

Limb lengthening surgery helps kids with dwarfism reach new heights

Putting on a pair of shoes is something many of us take for granted every day. But for 7-year-old... Read More