SHORT STATURE

Promising horizons in achondroplasia along with the development of new drugs

Ozono, K., Kubota, T., & Michigami, T. (2024). Promising horizons in achondroplasia along with the development of new drugs. Endocrine journal, 10.1507/endocrj.EJ24-0109. Advance online publication. https://doi.org/10.1507/endocrj.EJ24-0109 AFFILIATIONS ABSTRACT Achondroplasia (ACH) is…

U.S. Food and Drug Administration Approves BioMarin’s VOXZOGO® (vosoritide) for Children Under 5 Years with Achondroplasia

The following press release was obtained from BioMarin.com. To learn more about BioMarin, VOXZOGO®, vosorotide, and their other pipelines and research for achondroplasia and other skeletal dysplasias, click here. Expanded…

Achondroplasia · BioMarin

Novel therapy improves height for children with achondroplasia

via Healio/Endocrine Today Children with a common form of skeletal dysplasia saw persistent and sustained improvements in annualized growth velocity with an investigational analogue of C-type natriuretic peptide, according to…